The first FDA-approved gene therapy could cure inherited retinal defects.
The first gene therapy for children is coming to Europe.
A new breakthrough gene therapy could be made available to children suffering from a rare genetic disorder.
“If you could do one action that might save a thousand, a million or a billion people—but you might die from doing it? Why would you take the risk?”
Gene edited immune cells from a healthy donor saves the life of one-year-old child dying of leukemia.
Biotech startup Editas Medicine intends to begin using CRISPR in human trials to treat a rare form of blindness by 2017.
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